Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

Pfizer said on Thursday it will stop global development and commercialization of its hemophilia gene therapy, Beqvez, citing ...

Regeneron Pharmaceuticals said on Monday its experimental gene therapy showed improved hearing in 10 of 11 children between ...

Fuse Vectors has raised $5.2 million of funding as it moves closer to commercialising its innovative new approach to ...

Japan's regenerative medicine cold chain logistics market thrives on aging demographics, stringent regulations, and advanced ...

Revolutionary gene therapy approaches show promise in treating various retinal conditions, potentially transforming treatment ...

A gene therapy from Regeneron Pharmaceuticals Inc. improved hearing in nearly all deaf children in a clinical trial, results ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. | ...

Eleven children who were legally blind at birth all gained visual acuity after receiving MeiraGTx's investigational gene ...