Now, a study in Cell finds that some noncoding RNAs are not, in fact, junk—they are functional and play an important role in ...
A new type of therapy that 'edits' a gene in patients with a rare heart condition has been shown to be safe and effective, according to research from UCL and the Royal Free Hospital.
When the CRISPR Cas9 protein is added to a cell along with a piece of guide RNA, the Cas9 protein hooks up with the guide RNA and then moves along the strands of DNA until it finds and binds to a ...
A single treatment with a CRISPR-Cas9 based gene editing therapy is enough to replace the daily medication of patients with ...
This expert work will continue as the CRISPR-Cas9 therapy NTLA-2002 moves into the third phase of the clinical development program. This trial will include more patients and once again be executed ...