An Italian foundation that helped a young boy overcome Wiskott-Aldrich syndrome becomes the first non-profit in the world to ...
According to Moorfields Eye Hospital, the procedure consists of injecting healthy copies of the defective gene into the back ...
Fanconi Anaemia is caused by mutations in genes responsible for DNA repair. It is an autosomal recessive disorder, meaning ...
Gene therapy for another form of genetic blindness has been available on the NHS since 2020. The new work builds on that ...
A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic ...
A revolutionary gene therapy treatment in London has improved the vision of children suffering from a rare genetic disorder, ...
Four young children have gained life-changing improvements in sight following treatment with a pioneering new genetic ...
According to Moorfields Eye Hospital, the procedure consists of injecting healthy copies of the defective gene into the back of the eye, very early in life, in order to treat severe forms of the ...