Fuse Vectors has raised $5.2 million of funding as it moves closer to commercialising its innovative new approach to ...

Fanconi Anaemia is caused by mutations in genes responsible for DNA repair. It is an autosomal recessive disorder, meaning ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...

A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic ...

RNA-based therapeutics have rapidly emerged over the past decade, offering a new class of medicines that differ significantly from conventional drugs. These therapies can be programmed to target or ...

According to Moorfields Eye Hospital, the procedure consists of injecting healthy copies of the defective gene into the back ...