The genetic basis of Fanconi anemia (FA) is mysterious and complex, as none of the five genes previously associated with the disorder have homology to genes encoding proteins of known function.

The Redditor, who is battling liver cancer, mouth cancer, and a rare genetic condition, Fanconi Anemia, posted a heartfelt ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) shared encouraging updates on its Danon Disease Program through a recent investor ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today ...

Fanconi anemia has no known cure and can cause bone marrow failure and cancer. So Jimbo and his ex-wife, Candi Fisher, established the Kidz 1st Fund in 2011 to help spread awareness and raise ...

Analyst Eric Joseph of J.P. Morgan maintained a Buy rating on Rocket Pharmaceuticals (RCKT – Research Report), retaining the price target of ...

Rocket Pharma ( (RCKT) ) has released its Q3 earnings. Here is a breakdown of the information Rocket Pharma presented to its investors.Don't ...

RP-L102, which the firm designed to treat a form of disease caused by FANCA mutations, is already under review with the European Medicines Agency.