CRISPR is turned into a drug delivery system that helps recreate fetal hemoglobin, which then changes into red blood cells. Because the gene mutation for sickle cell disease is not found in fetal ...
Aruvant is developing ARU-1801 as a therapy designed to boost levels of functional fetal hemoglobin in β-thalassemia patients and restore normal red blood cell function. “At Aruvant ...
Some scientists are especially “interested in doing research with fetal liver because it’s a rich source of stem cells,” which can have important therapeutic applications, says Dr.
This oral medication is considered a first-line treatment for sickle cell disease, and can help reduce pain crises. Hydroxyurea causes the body to produce fetal hemoglobin, a type of hemoglobin ...
5 news release from the company. Data from the phase 1/2 Beacon trial indicated that Beam-101, the company’s sickle cell therapy, increased fetal hemoglobin levels from an initial range of 4% to ...
MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment of sickle cell disease, ...