FXS is a neurodevelopmental disorder caused by loss of the FMR1 encoded protein Fragile X Messenger Ribonucleoprotein (FMRP). It affects 1 in 7,000 males and 1 in 11,000 females and is the leading ...
The company’s broad portfolio targets multiple drivers of cancer, including a novel oncology discovery program focused on the fragile-X multifunctional RNA-binding protein (FMRP) and a ...