The U.S. Food and Drug Administration has approved Neurocrine Biosciences' drug to treat a type of genetic disorder, the ...

The Tbx1 gene influences brain volume and social behavior in autism and schizophrenia, with its deficiency linked to amygdala ...

Kanazawa University, have discovered how a protein called lamin A helps repair the protective barrier around a cell's DNA.

Two years ago, Alexa underwent a corpus callosotomy, a surgery to prevent seizures from spreading from one side of the brain ...

Through the Sing Me a Story Foundation, the two young brothers wrote a story together about a pair of dinosaur siblings and ...

The gene-editing technique is effective for treating some illnesses but it's been too expensive to consider it for rare ...

Neurocrine Biosciences won Food and Drug Administration approval late Friday for the first new treatment for an adrenal disease in decades.

Scientists have discovered a potential genetic link to Alzheimer's disease which could revolutionise how the condition is ...

Several rare immune disorders are caused by mutations in the patient's DNA. In a new study published in the Journal of ...

The Sink family in Sachse hosts 'Do It for Declan' 5K raising awareness and money for research into Sanfilippo syndrome, the ...

A groundbreaking study explores the overlooked X-chromosome’s role in Alzheimer’s disease, revealing seven genetic loci ...

Avidity Biosciences' AOC platform shows promising results for genetic diseases, making it a strong buy with potential upside ...