CRISPR gene editing tools can technically locate the mutated CFTR gene, break it, and provide DNA-based instructions for the ...
(D) CFTR: Cystic fibrosis transmembrane conductance regulator facilitates the transport of chloride ions across various cell membranes along with water (left). Mutated CFTR reduces the transport ...
This includes gene therapy, in which the mutated gene is supplemented by a healthy copy of CFTR, but the Foundation is also enthusiastic about technologies like CRISPR Cas9 to selectively correct ...