Shares of Agios Pharmaceuticals collapsed Monday on an unexpected side effect related to the company's thalassemia treatment, ...

Thalassemia is an inherited blood condition. When you have it, your body has fewer red blood cells and less of a protein called hemoglobin than it should. Hemoglobin is important because it lets ...

The treatment CS-101 uses innovative transformer Base Editing (tBE) technology to help people with severe diseases such as ...

The cumulative results of decades of work and advances in medicine are reflected in the increased survival of thalassaemia ...

Shares of Agios Pharmaceuticals AGIO lost 21% yesterday after management revealed that two thalassemia patients who received ...

Medical experts and thalassemia advocates are urging the Indian government to mandate nucleic acid amplification testing (NAT) for blood safety, create a national thalassemia control program ...

When you give to Light Up A Lawn, Light Up A Life, you are supporting programs like Nationwide Children's cutting-edge gene ...

ENERGIZE-T Study Achieved Primary and All Key Secondary Endpoints in Adult Patients with Transfusion-Dependent Alpha- or Beta-Thalassemia –– ...

In a report released yesterday, Alec Stranahan from Bank of America Securities reiterated a Buy rating on Agios Pharma (AGIO – Research ...

Two Saudi Arabian agencies signed on with Vertex Pharmaceuticals to help boost the countr | The Vertex agreement is part of ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced longer-term data for CASGEVY™ (exagamglogene autotemcel) from global clinical trial ...