Usher syndrome is a genetic disorder involving the loss of both sight and hearing. The hearing loss generally occurs at birth or shortly thereafter; while a progressive loss of vision due to retinitis ...
US FDA grants Orphan Drug Designation to AAVantgarde Bio’s AAVB-081 to treat Usher Syndrome Type 1B retinitis pigmentosa: Milan, Italy Tuesday, December 3, 2024, 16:00 Hrs [IST] ...
Individuals born with Usher syndrome type 1F do not have a sense of balance, cannot hear, and lose their vision over time. But scientists have now developed a gene therapy that could enable patients ...
People with Usher syndrome type 1F are born without hearing or a sense of balance and gradually lose their vision. The new approach restored hearing and balance in the mice.