In our study population, 78.3% of the patients with CF and 87.1% of the parents had no preexisting knowledge of the availability of DTC genetic testing for carrier status of genetic diseases ...

Introduction and Objectives Gene therapy for cystic fibrosis is approaching clinical trials. Using a lentiviral vector pseudotyped with Sendai virus fusion and hemagglutinin-neuraminidase proteins, ...

Join the inaugural Rock CF Thumb Coast Marathon on Nov. 2, 2025, in Michigan’s Thumb. Enjoy scenic coastal views and support ...

At the center of a new licensing deal is an experimental medicine, PTC518, which is currently being tested in a roughly ...

It’s a disease that few of us think about, but the American Lung Association says cystic fibrosis affects about 40,000 ...

Boston, Massachusetts-based Vertex Pharmaceuticals Incorporated (VRTX) develops and commercializes therapies for treating ...

Oct. 28, 2024 — Using state-of-the-art technology, researchers have identified several specific steps needed for CRISPR to become active and perform its gene editing function. These preclinical ...

Prime Medicine's strategic collaboration with Bristol Myers provided $55 million in cash upfront. Read why I upgrade PRME stock from hold to buy.

Newborn screening, conducted within the first 24-48 hours post-birth, identifies hidden genetic, metabolic, and endocrine ...

Nov. 22, 2024 — Geneticists have developed a gene drive-based solution to the widespread problem of insecticide resistance. In an effort to protect valuable crops, the researchers created an 'e ...

A gene that causes accelerated reproductive aging is directly tied to the risk of miscarriage in younger women, a new study ...

Katy López, the mother of six-year-old Yoslany Herrera López, is making a heartfelt plea for a humanitarian visa to enable ...