Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable ...

The Redditor, who is battling liver cancer, mouth cancer, and a rare genetic condition, Fanconi Anemia, posted a heartfelt ...

Ifosfamide (IFA) is a powerful chemotherapeutic drug that is active against a variety of paediatric malignancies. However, renal toxicities such as haemorrhagic cystitis and Fanconi syndrome are major ...

Jasper Therapeutics, Inc. (Nasdaq: JSPR) (Jasper), a clinical stage biotechnology company focused on development of ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) shared encouraging updates on its Danon Disease Program through a recent investor ...

It has three clinical-stage ex vivo lentiviral vector programs for fanconi anemia, a genetic defect in the bone marrow that reduces production of blood cells or promotes the production of faulty blood ...

Anemia Deficiency in the concentration of erythrocytes and/or hemoglobin concentration; further defined as a hematocrit or hemoglobin greater than 2 standard deviations below the mean for age and ...

Greater knowledge of neonatal erythrocytes will provide a framework within which to understand both the pathogenesis of anemia and the developmental changes that are taking place after birth.