In psychiatric conditions like autism spectrum disorder and schizophrenia, differences in social behavior correlate with ...
In a significant medical feat, Indian scientists have developed the first-in-human gene therapy using lentiviral vectors for ...
India has successfully conducted its first in-human gene therapy for hemophilia A, with patients experiencing no bleeding ...
Haemophilia is a severe bleeding disorder caused by the deficiency of clotting Factor VIII, leading to spontaneous internal ...
Expression Therapeutics, Inc., has presented the results of a Phase 1 clinical trial for its novel lentiviral vector-based gene therapy — ET3 — for hemophilia A at the Annual Meeting of the American ...
Current treatments require frequent Factor VIII replacement therapy, which faces challenges such as high costs, venous access ...
SPR301 is a potential best-in-class gene therapy candidate that delivers a more stable, rationally engineered version of GCase, the enzyme ...