Scientists in the UK have successfully used gene therapy to restore some vision to legally blind children with an inherited retinal condition. All 11 children in the clinical trial saw improvements ...

HAYWARD, CA, USA I February 28, 2025 I Avirmax Biopharma, Inc., a leader in developing the next generation of AAV gene therapies, today announced the ...

如今，来自NIHR Moorfields生物医学研究中心和伦敦大学学院的研究人员发现，基因治疗提高了患有 AIPL1 相关严重视网膜 营养不良 的幼儿的视力，并保留了视网膜结构。这是针对这种疾病的基因补充疗法的首次人体试验。