Scientists in the UK have successfully used gene therapy to restore some vision to legally blind children with an inherited retinal condition. All 11 children in the clinical trial saw improvements ...

MALVERN, PA — Ocugen, Inc. (NASDAQ: OCGN) announced a significant milestone with the U.S. Food and Drug Administration (FDA), ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

The vision of one child with AIPL1-associated severe retinal dystrophy improved from light perception to naming his favourite ...

Retinal gene therapy advancements may rewrite the book on treatments for age-related macular degeneration and diabetic eye diseases.

Reducing the number of intravitreal injections to treat age-related macular degeneration (AMD) is a top priority in current ...

A gene therapy treatment has enabled sight improvements for blind infants, through pioneering work by University College ...

Through this collaboration, Nanoscope Therapeutics will utilize Verana Health’s Qdata ® Retinitis Pigmentosa, which is a research-ready, real-world dataset that can be used to analyze patients with RP ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...

Preeminent retinal disease expert panel to support Alkeus’ development programs and scienceCAMBRIDGE, Mass., Feb. 25, 2025 (GLOBE NEWSWIRE) -- Alkeus Pharmaceuticals, Inc., a biopharmaceutical company ...

Four children born with a rare genetic form of severe blindness have all experienced significant improvements in their ...