Gene therapy with voretigene neparvovec-rzyl partially ... the patients' RT pathway remained strengthened even after the retinal intervention." "These findings not only provide useful ...
Aaron Nagiel treats the first patient at CHLA with Luxturna retinal gene therapy in 2017. In 2024, Dr. Nagiel's team celebrated its 100th Luxturna procedure. (Photo: Business Wire) There’s no ...
It is focusing on retinal diseases, with its most advanced ... to legal blindness when they reach their early forties. The gene therapy was acquired from US biotech AGTC in 2022 by Syncona ...