Fuse Vectors has raised $5.2 million of funding as it moves closer to commercialising its innovative new approach to ...

Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

A study led by UMass Chan Medical School researchers has demonstrated that a gene therapy to correct a mutation that causes ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Before the therapy, the affected children were legally blind, only able to distinguish between light and dark. However, after ...

Danish start-up Fuse Vectors has received $5.2 million in preseed financing to further develop their gene therapy technology.

AAV-Navβ1 gene therapy effectively reduces seizures and prolongs life in a mouse model of SCN1B-linked Dravet syndrome, ...

Gene therapy, the idea of fixing faulty genes ... activity and is small enough to be packaged within a non-pathogenic virus that can deliver ...

Eleven children who were legally blind at birth all gained visual acuity after receiving MeiraGTx's investigational gene ...

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...