A study led by UMass Chan Medical School researchers has demonstrated that a gene therapy to correct a mutation that causes ...

The 7 major adeno-associated virus gene therapy market reached a value of USD 2.7 Billion in 2024. Looking forward, IMARC Group expects the 7MM to reach USD 107.2 Billion by 2035, exhibiting a growth ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Four young children have gained life-changing improvements in sight following treatment with a pioneering new genetic ...

The toddlers were treated using gene therapy, through which patients are given a harmless virus containing healthy versions of a defective gene in order to remedy the problem. “Gene therapy ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

A gene therapy treatment has enabled sight improvements for blind infants, through pioneering work by University College ...

Gene therapy is usually reserved for severe and ... that scavenge foreign proteins, viruses and bacteria, and rapidly (within 3 hours) transport these foreign agents to the immune cells within ...

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

Gene therapy involves the introduction of new genes ... In a recently reported study, a novel engineered oncolytic Newcastle disease virus encoding porcine α1,3-galactosyltransferase was ...

Ten out of 11 children with a form of congenital deafness who were treated with an experimental gene therapy developed by ...