Complete SAD/MAD data from the Phase 1 trial of DISC-3405 in healthy volunteers were presented. In the SAD portion of this trial, healthy males and females ages 18 to 65 were given a single dose of ...
Thalassemia is a condition in which the body makes less hemoglobin, a protein that's an important part of red blood cells. This results in red blood cells being destroyed, which is known as hemolytic ...
Thalassemia is a rare inherited blood disorder caused by genetic mutations that lead to a reduced production of healthy hemoglobin, compromising red blood cell development, health and survival, and ...