Complete SAD/MAD data from the Phase 1 trial of DISC-3405 in healthy volunteers were presented. In the SAD portion of this trial, healthy males and females ages 18 to 65 were given a single dose of ...
Thalassemia is a condition in which the body makes less hemoglobin, a protein that's an important part of red blood cells. This results in red blood cells being destroyed, which is known as hemolytic ...
The goal is to illustrate how RBC indices and characteristics are used in the diagnosis of a neonate or young infant with anemia. A brief review of hemoglobin synthesis and postnatal changes in ...
The AURORA study is a randomized, double-blind, placebo-controlled Phase 2 clinical trial that enrolled 75 adult subjects with EPP. Subjects were randomized 1:1:1 to receive 20 mg of bitopertin (n=26) ...