Also called Tennesee fainting goats, myotonic goats are an American breed that is famous for becoming stiff as a board when they get overly excited or scared. They are popular as pets due to their ...

With its recent data drop for an oligonucleotide candidate, Dyne Therapeutics signals it may become a frontrunner in this ...

NEW BRIGHTON, MINN. — Twenty-year-old Giacomo Naylor, 16-year-old Lukas Naylor, 13-year-old Isadora Naylor and Gianna Naylor were all born with myotonic dystrophy — a genetic disorder that ...

In recent years, a growing understanding of myotonic dystrophy type 1 (DM1)—an often fatal, devastating, rare neuromuscular disorder that causes muscle weakness and other life-limiting ...

About Myotonic Dystrophy Type 1 (DM1) DM1 is a rare, progressive, genetic disease that affects skeletal, cardiac and smooth muscle. It is a monogenic, autosomal dominant disease caused by an ...

Data from DELIVER and ACHIEVE Clinicals Trial to be Presented - - Presentation on ACHIEVE Trial in DM1 and Company Symposium to Feature Data on the Use of Splicing Correction as a Prognostic Biomarker ...