As Rare Disease Day is commemorated on 28 February, experts discuss the barriers to gene therapy access for some rare ...

For the 20 million rare disease patients in China, accurate diagnoses, timely treatment, and affordable medications are shared goals. As the country makes significant strides in tackling rare diseases ...

Full year 2024 revenue of $807 million, exceeding guidance - - All 2024 clinical and regulatory milestones were achieved on schedule, including four NDA submissions ...

Alltrna’s CEO Michelle Warner said that the approach allows for basket trials that can group patients with different diseases ...

A Group, Massive Awareness for Rare Diseases (MARD) Nigeria, yesterday, visited markets in the Igbona area of Osogbo, the capital of Osun State, to create awareness on rare diseases and advocate for ...

“L-tyrosine is a precursor to dopamine, the neurotransmitter that aids in motivation, mood regulation, and pleasure,” says ...

A group, Massive Awareness for Rare Diseases (MARD) Nigeria, on Thursday, visited markets in the Igbona area of Osogbo, the ...

Five Tufts faculty have been named as senior members of the National Academy of Inventors, an honor for academic inventors ...

Galen Limited, a leading pharmaceutical sales and marketing company, has announced a significant step in its global expansion by signing an exclusive licensing agreement with Taiwan-based Bora Health ...

"Potential effects have been described that need to be investigated by more and better studies.” Inquiry about the safety of ...

TD Cowen initiated coverage of Maze Therapeutics (MAZE) with a Buy rating and no price target The company’s MZE829, and oral APOL1 inhibitor, ...

NIMS Medical Genetics department in Hyderabad offers cutting-edge diagnostic and therapeutic services for rare genetic ...