Mikey Oliveri was born too small for any existing pacemaker options. Doctors turned to an innovative, adapted option.

There's a window of time in our lives we've all passed through yet still know so little about: early gestation.

■ ...

A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...

Title: Impact of the Enzyme Replacement Therapy, INZ-701, in Children with ENPP1 Deficiency: Experience from an Expanded Access Program Presentation Number: 10 – Poster Session Date: Saturday, ...