Beam Therapeutics reported promising trial data from seven sickle cell patients treated with their gene-edited therapy, ...
Beam Therapeutics (BEAM) announced new data for its Engineered Stem Cell Antibody Evasion, or ESCAPE, conditioning platform.
This results in red blood cells being destroyed, which is known as hemolytic anemia ... People with beta thalassemia trait will have elevation in hemoglobin A2 and/or F (fetal). There is no simple ...
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced longer-term data for CASGEVY™ (exagamglogene autotemcel) from global clinical trial ...
A drug developed by Sanofi raised platelet counts and reduced bleeding episodes in patients with a rare autoimmune disorder ...
Though he doesn't remember it, Branden Baptiste had his first sickle cell crisis at age 2. Through elementary school, he was ...
Though he doesn't remember it, Branden Baptiste had his first sickle cell crisis at age 2. Through elementary school, he was ...
MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment of sickle cell disease, ...
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Sickle Cell Anemia Symptoms
The hallmark symptom of sickle cell anemia is pain, particularly episodes of sudden pain, sometimes called sickle cell crises ...
The systemic agent is the first approved by the FDA for patients with NSCLC or pancreatic adenocarcinoma harboring an NRG1 gene fusion.
Sites in Los Angeles and near San Francisco California are enrolling people with severe SCD for a trial to test a gene ...
HIBISCUS phase 2 data evaluating the safety profile and efficacy of etavopivat in adult and adolescent patients with sickle ...