This results in red blood cells being destroyed, which is known as hemolytic anemia ... People with beta thalassemia trait will have elevation in hemoglobin A2 and/or F (fetal). There is no simple ...
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced longer-term data for CASGEVY™ (exagamglogene autotemcel) from global clinical trial ...
MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment of sickle cell disease, ...