Pfizer’s bet on gene therapies in haemophilia has been a bust
Pfizer has ended the global commercialisation of its haemophilia B (factor IX deficiency) gene therapy Beqvez, citing soft ...
Blind Children See for the First Time Thanks to a Revolutionary Gene Therapy
A groundbreaking gene therapy has restored sight in four young children born with severe blindness due to a rare genetic ...
GlobalData on MSN5d
Success for YolTech’s hyperoxaluria in vivo gene therapy in early-stage trial
YolTech's gene therapy is intended as a one-time life-long cure for patients living with PH1, which can lead to kidney ...
Gene Therapy Market to Hit USD 36.55 Billion by 2032 with 19.4% CAGR | MarketsandMarkets™.
The global Gene Therapy market, valued at US$7.21 billion in 2023, is forecasted to grow at a robust CAGR of 19.4%, reaching ...
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Gene Therapy News
Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...
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Genetic therapy gives infants life-changing improvements in sight
The children were born with a severe impairment to their sight due to a rare genetic deficiency that affects the AIPL1 gene. The condition, a form of retinal dystrophy, means those affected are ...
Medindia8d
Genetic Therapy Restores Sight in Infants
Four young children have gained life-changing improvements in sight following treatment with a pioneering new genetic ...
New Atlas9d
Infant's genetic muscle disorder improved by treating pregnant mother
Spinal muscular atrophy (SMA) is a debilitating genetic condition that’s usually fatal by a few years of age. But an ...