With access to major transportation hubs like Philadelphia International Airport and the Amtrak Northeast Corridor, the city provides direct connections to other life sciences communities such as ...

New research shows people in specific Polynesian communities have a much higher rate of a form of Parkinson’s disease considered rare elsewhere.

Children with a rare form of eye disorder who were born blind can now see thanks to a "remarkable" gene therapy breakthrough.

Qure's AMT-130 shows 80% Huntington's progress reduction, eyeing FDA approval. Click here to read why I rate QURE stock a Buy ...

Jace’s mum DJ, 35, told the PA news agency: “Pre-surgery, at around two years old, you could have held up any object, even a ...

Medics in the UK have become the first in the world to successfully administer a pioneering gene therapy that preserves sight in young children with an extremely rare genetic condition that usually ...

Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...

CRISPR epigenome editing successfully reactivates silenced genes in Prader-Willi Syndrome, highlighting potential for ...