With its recent data drop for an oligonucleotide candidate, Dyne Therapeutics signals it may become a frontrunner in this ...

The 6-minute walking exercise leads to key gait changes including spatiotemporal changes in patients with myotonic dystrophy type 1, according to a new study published in the scientific journal ...

Myotonic dystrophy type 1 (DM1) is the most common muscular dystrophy that affects multiple systems including the muscle and heart. The mutant CTG expansion at the 3′-UTR of the DMPK gene causes the ...

Methods: 598 patients with a neuromuscular disease were studied (139 with facioscapulohumeral dystrophy, 322 with adult onset myotonic dystrophy, and 137 with hereditary motor and sensory neuropathy ...

An NHS hospital has apologised after the 'completely avoidable' death of a 'full of life' schoolgirl. The heartbroken family ...

An NHS apology has been issued to the family of a 'full of life' schoolgirl whose death was deemed to be 'completely ...

Background: Myotonic dystrophy type 1 is a slowly progressive multisystem disease in which skeletal muscle involvement is prominent. As novel physical and pharmacological treatments become available, ...

A hospital has apologised after errors contributed to the death of a 15-year-old girl in its care. Isla Mae Hudson, from ...

Reduced renal function has been described in the genetic muscle wasting disorder myotonic dystrophy type 1 (DM1). However, the mechanism for kidney involvement in DM1 is unknown and its relationship ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced management participation in three upcoming investor ...