As Rare Disease Day is commemorated on 28 February, experts discuss the barriers to gene therapy access for some rare ...

Synthetic biology specialist Synlogic will start phase 3 testing of a drug for rare metabolic disorder phenylketonuria (PKU) next year, after reporting solid proof-of-concept data.

“L-tyrosine is a precursor to dopamine, the neurotransmitter that aids in motivation, mood regulation, and pleasure,” says ...

NIMS Medical Genetics department in Hyderabad offers cutting-edge diagnostic and therapeutic services for rare genetic ...

A visitor tries a surgery robot at the booth of Fosunpharma at the Medical Equipment & Healthcare Products Exhibition Area ...

Alltrna’s CEO Michelle Warner said that the approach allows for basket trials that can group patients with different diseases ...

Galen Limited, a leading pharmaceutical sales and marketing company, has announced a significant step in its global expansion by signing an exclusive licensing agreement with Taiwan-based Bora Health ...

When Ms. Liu, a cancer patient, picked up a box of medication at the hospital pharmacy, she felt an overwhelming sense ...

A Group, Massive Awareness for Rare Diseases (MARD) Nigeria, yesterday, visited markets in the Igbona area of Osogbo, the capital of Osun State, to create awareness on rare diseases and advocate for ...

A group, Massive Awareness for Rare Diseases (MARD) Nigeria, on Thursday, visited markets in the Igbona area of Osogbo, the ...

TD Cowen initiated coverage of Maze Therapeutics (MAZE) with a Buy rating and no price target The company’s MZE829, and oral APOL1 inhibitor, ...

Trillions of microbes live inside us. Many are helpful; others, not so much. Over the last 15 years MIT has played a central ...