As Rare Disease Day is commemorated on 28 February, experts discuss the barriers to gene therapy access for some rare ...

Synthetic biology specialist Synlogic will start phase 3 testing of a drug for rare metabolic disorder phenylketonuria (PKU) next year, after reporting solid proof-of-concept data.

Considering taking supplements to treat phenylketonuria pku? Below is a list of common natural remedies used to treat or reduce the symptoms of phenylketonuria pku. Follow the links to read common ...

The drug is supposed to treat phenylketonuria, a disease that can result in brain and nerve damage if not addressed. A laboratory technician in a safety suit analyzing and conducting a series of ...