By harnessing the unique auditory capabilities of these insects, scientists hope to revolutionize the capabilities of ...

Methods to improve the distribution of enzymes that are injected or expressed from transduced cells will be required for many human brain therapies. Recent studies showed that a peptide ...

For the latter disease, it was reasoned that treatment should be done in the absence of ERT to maintain the transduced progenitor cells' growth advantage. Figure 2: Gene therapy for SCID-X1 and ...

Prof. Chengcai Chu and his team from South China Agricultural University have systematically summarized the process of ...

A woman diagnosed with neuroblastoma in childhood has remained in remission for more than 18 years after being treated with ...

This study presents an optimized CRISPR-Cas12a system for large-scale genetic screening, revealing critical genes involved in lymphoma development and therapy.

Organoids were cultured from healthy donor iPSC sources and differentiated using the human iPSC-derived Cerebral Organoid ...

Myeloid deficiency of the mitochondrial transacetylase tafazzin upregulates mtROS, disrupting UPR and calcium homeostasis, ...

This important study characterizes and validates a new activity marker - fast labelling of engram neurons (FLEN) - which is transiently active and driven by cFos, allowing the monitoring of intrinsic ...

RNA-based therapeutics have rapidly emerged over the past decade, offering a new class of medicines that differ significantly from conventional drugs. These therapies can be programmed to target or ...

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