Japan's regenerative medicine cold chain logistics market thrives on aging demographics, stringent regulations, and advanced ...

Scientists compared five families and multiple generations to find a gene variant that prevents COPA Syndrome and opens the door to a new gene therapy for the condition.

Ten children who received DB-OTO for profound genetic hearing loss due to variants of the otoferlin gene showed notable ...

Solid Biosciences reported recent positive data in developing their gene therapy candidate SGT-003. The phase 1/2 INSPIRE ...

Sarepta Therapeutics, Inc. SRPT reported fourth-quarter 2024 earnings per share (EPS) of $1.50, which missed the Zacks ...

New Biotech labs are coming to Roanoke after the city received $4 million in the state budget passed by the Virginia General ...

A rare genetic disease that ravages some but spares others has baffled researchers — until now. Researchers found that a ...

ClearPoint's Q4 updates: neurosurgery growth, expanding services, controlled cash burn and high-potential partner programs ...

What’s it like reporting on the FDA during the early and turbulent weeks of the Trump administration? Why did Bluebird Bio ...

Techne's strong growth in Protein Sciences & Spatial Biology despite market pressure. Explore more details here.

During his visit to the Kingdom of Bahrain, the Director-General of the World Health Organization (WHO), Dr. Tedros Adhanom ...

The Muscular Dystrophy Association (MDA) announced today that Robert Califf, MD, MAAC, former Commissioner of the U.S. Food ...