Metachromatic leukodystrophy is a genetic condition that occurs due to an enzyme deficiency. Patients with this disorder have ...
The Metachromatic Leukodystrophy Initiative (MLDi) critically responds to the findings of Zhang et al. on lentivirus-modified hematopoietic stem cell gene therapy in three metachromatic leukodystrophy ...
The bill considered today was aimed at forcing more transparency in the attorney general's office and failed on a 67 to 65 ...
This drug treats a debilitating and lethal disease that mostly affects infants called metachromatic leukodystrophy (MLD). Children affected by this very rare genetic disease that affects the brain ...