Columnist Robin Stemple knows his walker should help prevent falls, but it didn't work out that way on a simple maneuver to ...

Based on the positive findings from the Phase 1/2 study, Genethon is planning to launch Phase 3 testing of GNT0004 next year.

Columnist Patrick Moeschen, who lives with limb-girdle muscular dystrophy, explains why controlling what he can is so ...

Regenxbio hopes to use the study's results to ask the U.S. Food and Drug Administration to grant accelerated approval to the ...

As a caregiver for three sons with DMD, columnist Betty Vertin clung to her many responsibilities. This year she's learned to let go a bit.